Addressing Unmet Needs for Patients With Spinal Muscular Atrophy—Understanding Patient Challenges and Management Approaches

Release Date: October 31, 2025

Expiration Date: October 31, 2026

Activity Overview

Spinal muscular atrophy (SMA) is a rare progressive neuromuscular disease that profoundly impacts patients and their families. Over the past decade, remarkable advances in genetic testing, disease-modifying therapies, and multidisciplinary care have transformed the outlook for individuals living with SMA. However, timely diagnosis, optimal treatment selection, and coordinated long-term management remain ongoing challenges.

In this interactive educational forum, participants can review the pathophysiology and disease burden of SMA with a focus on early recognition and diagnosis, explore current and emerging therapies and their implications for clinical practice, and survey multidisciplinary care strategies to address motor, respiratory, nutritional, and psychosocial needs. Participants will gain insight into the rapidly evolving treatment landscape and explore strategies for advancing care and improving outcomes for patients and families affected by this rare disease.

This educational activity is an archive of the live virtual symposium held on September 27, 2025.

Target Audience

This educational activity is directed toward neuromuscular disease specialists, neurologists, specialty nurse practitioners, specialty physician assistants, nurses, and other health care providers involved in the care of patients with neuromuscular diseases.

Learning Objectives

Upon successful completion of this activity, you should be better prepared to:

• Identify the burden of disease of spinal muscular atrophy (SMA)
• Analyze clinical trial data for disease-modifying therapies for SMA
• Apply strategies to optimize the transition of care for patients with SMA